Ataluren Translarna® |
Formulary
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NICE HST22: Ataluren for treating Duchenne muscular dystrophy with a nonsense mutation in the dystrophin gene |
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Ravulizumab Ultomiris® |
Non Formulary
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NICE TA940: Ravulizumab for treating generalised myasthenia gravis (terminated appraisal) NICE TA941: Ravulizumab for treating AQP4 antibody-positive neuromyelitis optica spectrum disorder (terminated appraisal) |
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Satralizumab Enspryng® |
Non Formulary
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NICE TA960: Satralizumab for preventing relapses in neuromyelitis optica spectrum disorders |
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